• 13696 Citations
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1986 …2018
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Research Output 1986 2018

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Article
2018

Amelioration of Muscle and Nerve Pathology in LAMA2 Muscular Dystrophy by AAV9-Mini-Agrin

Qiao, C., Dai, Y., Nikolova, V. D., Jin, Q., Li, J., Xiao, B., Li, J., Moy, S. S. & Xiao, X., Jun 15 2018, In : Molecular Therapy - Methods and Clinical Development. 9, p. 47-56 10 p.

Research output: Contribution to journalArticle

Agrin
Muscular Dystrophies
Therapeutic Uses
Pathology
Muscles
2 Citations

A Retrospective Study of the Cytokine Profile Changes in Mice with FVIII Inhibitor Development after Adeno-Associated Virus-Mediated Gene Therapy in a Hemophilia A Mouse Model

Sun, J., Yuan, Z., Abajas, Y. L., Szollosi, D. E., Hu, G., Hua, B., Xiao, X. & Li, C., Mar 1 2018, In : Human Gene Therapy. 29, 3, p. 381-389 9 p.

Research output: Contribution to journalArticle

Dependovirus
Factor VIII
Hemophilia A
Genetic Therapy
Retrospective Studies

Lymphotoxin β receptor-mediated NFΚB signaling promotes glial lineage differentiation and inhibits neuronal lineage differentiation in mouse brain neural stem/progenitor cells

Xiao, X., Putatunda, R., Zhang, Y., Soni, P. V., Li, F., Zhang, T., Xin, M., Luo, J. J., Bethea, J. R., Cheng, Y. & Hu, W., Feb 20 2018, In : Journal of Neuroinflammation. 15, 1, 49

Research output: Contribution to journalArticle

Lymphotoxin beta Receptor
Lymphotoxin-alpha
Neural Stem Cells
Neuroglia
Transgenic Mice

MicroRNA-206 Downregulation Improves Therapeutic Gene Expression and Motor Function in mdx Mice

Bulaklak, K., Xiao, B., Qiao, C., Li, J., Patel, T., Jin, Q., Li, J. & Xiao, X., Sep 7 2018, In : Molecular Therapy - Nucleic Acids. 12, p. 283-293 11 p.

Research output: Contribution to journalArticle

Inbred mdx Mouse
MicroRNAs
Down-Regulation
Gene Expression
Muscles

Neonatal Systemic AAV-Mediated Gene Delivery of GDF11 Inhibits Skeletal Muscle Growth

Jin, Q., Qiao, C., Li, J., Li, J. & Xiao, X., Apr 4 2018, In : Molecular Therapy. 26, 4, p. 1109-1117 9 p.

Research output: Contribution to journalArticle

Dependovirus
Viral Genes
Skeletal Muscle
Growth
Forelimb
1 Citations

Overexpression of Mutant FKRP Restores Functional Glycosylation and Improves Dystrophic Phenotype in FKRP Mutant Mice

Tucker, J. D., Lu, P. J., Xiao, X. & Lu, Q. L., Jun 1 2018, In : Molecular Therapy - Nucleic Acids. 11, p. 216-227 12 p.

Research output: Contribution to journalArticle

Glycosylation
Dystroglycans
Phenotype
Mutation
Muscular Dystrophies

Recombinant Adeno-Associated Virus-Mediated Delivery of MicroRNA-21-3p Lowers Hypertension

Wang, F., Fang, Q., Chen, C., Zhou, L., Li, H., Yin, Z., Wang, Y., Zhao, C. X., Xiao, X. & Wang, D. W., Jun 1 2018, In : Molecular Therapy - Nucleic Acids. 11, p. 354-366 13 p.

Research output: Contribution to journalArticle

Dependovirus
MicroRNAs
Hypertension
Inbred SHR Rats
Vascular Smooth Muscle
2017

Adeno-Associated Virus–Mediated Mini-Agrin Delivery Is Unable to Rescue Disease Phenotype in a Mouse Model of Limb Girdle Muscular Dystrophy Type 2I

Vannoy, C. H., Zhou, H., Qiao, C., Xiao, X., Bang, A. G. & Lu, Q. L. Feb 1 2017 In : American Journal of Pathology. 187, 2, p. 431-440 10 p.

Research output: Contribution to journalArticle

Agrin
Dependovirus
Phenotype
Dystroglycans
Laminin
2 Citations

Efficacy of Gene Therapy Is Dependent on Disease Progression in Dystrophic Mice with Mutations in the FKRP Gene

Vannoy, C. H., Xiao, W., Lu, P., Xiao, X. & Lu, Q. L., Jun 16 2017, In : Molecular Therapy - Methods and Clinical Development. 5, p. 31-42 12 p.

Research output: Contribution to journalArticle

3 Citations

Follistatin N terminus differentially regulates muscle size and fat in vivo

Zheng, H., Qiao, C., Tang, R., Li, J., Bulaklak, K., Huang, Z., Zhao, C., Dai, Y., Li, J. & Xiao, X., Sep 15 2017, In : Experimental & molecular medicine. 49, 9, p. e377

Research output: Contribution to journalArticle

Follistatin
Fats
Muscles
Myostatin
Activins
46 Citations

In Vivo Excision of HIV-1 Provirus by saCas9 and Multiplex Single-Guide RNAs in Animal Models

Yin, C., Zhang, T., Qu, X., Zhang, Y., Putatunda, R., Xiao, X., Li, F., Xiao, W., Zhao, H., Dai, S., Qin, X., Mo, X., Young, W. B., Khalili, K. & Hu, W., May 3 2017, In : Molecular Therapy. 25, 5, p. 1168-1186 19 p.

Research output: Contribution to journalArticle

2016
3 Citations

Effect of Resveratrol-Based Nutritional Supplement on Choroidal Thickness: A Pilot Study

Wang, S., Moonasar, N., Xiao, X., Yin, T., Weinreb, R. N. & Sun, X., Feb 11 2016, (Accepted/In press) In : Current Eye Research. p. 1-7 7 p.

Research output: Contribution to journalArticle

Placebos
Optical Coherence Tomography
Control Groups
Nose
Vasodilation
2015
29 Citations

Adeno-associated virus type 2 and hepatocellular carcinoma?

Berns, K. I., Byrne, B. J., Flotte, T. R., Gao, G., Hauswirth, W. W., Herzog, R. W., Muzyczka, N., Vandendriessche, T., Xiao, X., Zolotukhin, S. & Srivastava, A., Dec 1 2015, In : Human Gene Therapy. 26, 12, p. 779-781 3 p.

Research output: Contribution to journalArticle

14 Citations

Enhanced transgene expression from recombinant single-stranded D-sequence-substituted adeno-associated virus vectors in human cell lines in vitro and in murine hepatocytes in vivo

Ling, C., Wang, Y., Lu, Y., Wang, L., Jayandharan, G. R., Aslanidi, G. V., Li, B., Cheng, B., Ma, W., Lentz, T., Ling, C., Xiao, X., Jude Samulski, R., Muzyczka, N. & Srivastava, A., Jan 1 2015, In : Journal of Virology. 89, 2, p. 952-961 10 p.

Research output: Contribution to journalArticle

Dependovirus
human cell lines
Terminal Repeat Sequences
Transgenes
hepatocytes
3 Citations

GRAF1 deficiency blunts sarcolemmal injury repair and exacerbates cardiac and skeletal muscle pathology in dystrophin-deficient mice

Lenhart, K. C., O'Neill, T. J., Cheng, Z., Dee, R., Demonbreun, A. R., Li, J., Xiao, X., McNally, E. M., Mack, C. P. & Taylor, J. M., Aug 21 2015, In : Skeletal Muscle. 5, 1, 27

Research output: Contribution to journalArticle

Focal Adhesion Kinase 1
Dystrophin
Nonpenetrating Wounds
GTP Phosphohydrolases
Myocardium
12 Citations

Loss-of-function PTPRD mutations lead to increased STAT3 activation and sensitivity to STAT3 inhibition in head and neck cancer

Peyser, N. D., Du, Y., Li, H., Lui, V., Xiao, X., Chan, T. A. & Grandis, J. R., Aug 12 2015, In : PloS one. 10, 8, e0135750

Research output: Contribution to journalArticle

Class 2 Receptor-Like Protein Tyrosine Phosphatases
protein-tyrosine-phosphatase
Head and Neck Neoplasms
Chemical activation
squamous cell carcinoma
5 Citations

Overcoming insulin insufficiency by forced follistatin expression in β-cells of db/db mice

Zhao, C., Qiao, C., Tang, R. H., Jiang, J., Li, J., Martin, C. B., Bulaklak, K., Li, J., Wang, D. W. & Xiao, X., May 9 2015, In : Molecular Therapy. 23, 5, p. 866-874 9 p.

Research output: Contribution to journalArticle

Follistatin
Insulin
Pancreas
Cell Proliferation
Myostatin
28 Citations

The systemic delivery of an oncolytic adenovirus expressing decorin inhibits bone metastasis in a mouse model of human prostate cancer

Xu, W., Neill, T., Yang, Y., Hu, Z., Cleveland, E., Wu, Y., Hutten, R., Xiao, X., Stock, S. R., Shevrin, D., Kaul, K., Brendler, C., Iozzo, R. V. & Seth, P., Mar 9 2015, In : Gene Therapy. 22, 3, p. 247-256 10 p.

Research output: Contribution to journalArticle

Decorin
Adenoviridae
Prostatic Neoplasms
Neoplasm Metastasis
Bone and Bones
2014
15 Citations

Adeno-associated virus-mediated overexpression of LARGE rescues α-dystroglycan function in dystrophic mice with mutations in the fukutin-related protein

Vannoy, C. H., Xu, L., Keramaris, E., Lu, P., Xiao, X. & Lu, Q. L., Jun 1 2014, In : Human Gene Therapy Methods. 25, 3, p. 187-196 10 p.

Research output: Contribution to journalArticle

Dystroglycans
Dependovirus
Glycosylation
Mutation
Genes
15 Citations

An AAV9 coding for frataxin clearly improved the symptoms and prolonged the life of Friedreich ataxia mouse models

Gérard, C., Xiao, X., Filali, M., Coulombe, Z., Arsenault, M., Couet, J., Li, J., Drolet, M. C., Chapdelaine, P., Chikh, A. & Tremblay, J. P., Jan 8 2014, In : Molecular Therapy - Methods and Clinical Development. 1, 1 p.

Research output: Contribution to journalArticle

Friedreich Ataxia
MM Form Creatine Kinase
Dependovirus
Phosphopyruvate Hydratase
Genes
41 Citations

Frequent mutation of receptor protein tyrosine phosphatases provides a mechanism for STAT3 hyperactivation in head and neck cancer

Lui, V. W. Y. , Peyser, N. D. , Ng, P. K. S. , Hritz, J. , Zeng, Y. , Lu, Y. , Li, H. , Wang, L. , Gilbert, B. R. , General, I. J. , Bahar, I. , Ju, Z. , Wang, Z. , Pendleton, K. P. , Xiao, X. , Du, Y. , Vries, J. K. , Hammerman, P. S. , Garraway, L. A. , Mills, G. B. & 2 others Johnson, D. E. & Grandis, J. R., Jan 21 2014, In : Proceedings of the National Academy of Sciences of the United States of America. 111, 3, p. 1114-1119 6 p.

Research output: Contribution to journalArticle

Protein Tyrosine Phosphatases
Head and Neck Neoplasms
Mutation
Receptor-Like Protein Tyrosine Phosphatases
Exome
11 Citations

GRAF1 promotes ferlin-dependent myoblast fusion

Lenhart, K. C., Becherer, A. L., Li, J., Xiao, X., McNally, E. M., Mack, C. P. & Taylor, J. M., Jan 1 2014, In : Developmental Biology. 393, 2, p. 298-311 14 p.

Research output: Contribution to journalArticle

Myoblasts
Muscles
Actins
Membranes
Skeletal Muscle Fibers
13 Citations

Intratumoral decorin gene delivery by AAV vector inhibits brain glioblastomas and prolongs survival of animals by inducing cell differentiation

Ma, H. I., Hueng, D. Y., Shui, H. A., Han, J. M., Wang, C. H., Lai, Y. H., Cheng, S. Y., Xiao, X., Chen, M. T. & Yang, Y. P., Mar 12 2014, In : International Journal of Molecular Sciences. 15, 3, p. 4393-4414 22 p.

Research output: Contribution to journalArticle

Decorin
Glioblastoma
genes
brain
animals
4 Citations

K137R Mutation on adeno-associated viral capsids had minimal effect on enhancing gene delivery in vivo

Qiao, C., Li, C., Zhao, C., Li, J., Bian, T., Grieger, J., Li, J., Samulski, R. J. & Xiao, X., Feb 1 2014, In : Human gene therapy methods. 25, 1, p. 33-39 7 p.

Research output: Contribution to journalArticle

Capsid
Mutation
Lac Operon
Luciferases
Transgenes
14 Citations

Muscle and heart function restoration in a limb girdle muscular dystrophy 2I (LGMD2I) mouse model by systemic FKRP gene delivery

Qiao, C., Wang, C. H., Zhao, C., Lu, P., Awano, H., Xiao, B., Li, J., Yuan, Z., Dai, Y., Martin, C. B., Li, J., Lu, Q. & Xiao, X., Jul 22 2014, In : Molecular Therapy. 22, 11, p. 1890-1899 10 p.

Research output: Contribution to journalArticle

Limb-Girdle Muscular Dystrophies
Myocardium
Walker-Warburg Syndrome
Dystroglycans
Genetic Therapy
2013
29 Citations

Adeno-associated Virus 9 mediated FKRP gene therapy restores functional glycosylation of α-dystroglycan and improves muscle functions

Xu, L., Lu, P. J., Wang, C. H., Keramaris, E., Qiao, C., Xiao, B., Blake, D. J., Xiao, X. & Lu, Q. L., Jan 1 2013, In : Molecular Therapy. 21, 10, p. 1832-1840 9 p.

Research output: Contribution to journalArticle

Walker-Warburg Syndrome
Dystroglycans
Dependovirus
Muscular Dystrophies
Glycosylation
20 Citations

Mouse models of fukutin-related protein mutations show a wide range of disease phenotypes

Blaeser, A., Keramaris, E., Chan, Y. M., Sparks, S., Cowley, D., Xiao, X. & Lu, Q. L., Aug 1 2013, In : Human genetics. 132, 8, p. 923-934 12 p.

Research output: Contribution to journalArticle

Phenotype
Mutation
Walker-Warburg Syndrome
Glycosylation
Muscular Dystrophies
22 Citations

Pentamethylquercetin protects against diabetes-related cognitive deficits in diabetic goto-kakizaki rats

Li, X. H., Xin, X., Wang, Y., Wu, J. Z., Jin, Z. D., Ma, L. N., Nie, C. J., Xiao, X., Hu, Y. & Jin, M. W., Jan 1 2013, In : Journal of Alzheimer's Disease. 34, 3, p. 755-767 13 p.

Research output: Contribution to journalArticle

Cyclic AMP Response Element-Binding Protein
Dendritic Spines
Insulin Resistance
Neurons
Glucose
5 Citations

Persistence, localization, and external control of transgene expression after single injection of adeno-associated virus into injured joints

Lee, H. H., O'Malley, M. J., Friel, N. A., Payne, K. A., Qiao, C., Xiao, X. & Chu, C. R., Apr 1 2013, In : Human gene therapy. 24, 4, p. 457-466 10 p.

Research output: Contribution to journalArticle

Dependovirus
Transgenes
Joints
Injections
Luciferases
2012
82 Citations

Canine models of Duchenne muscular dystrophy and their use in therapeutic strategies

Kornegay, J. N., Bogan, J. R., Bogan, D. J., Childers, M. K., Li, J., Nghiem, P., Detwiler, D. A., Larsen, C. A., Grange, R. W., Bhavaraju-Sanka, R. K., Tou, S., Keene, B. P., Howard, J. F., Wang, J., Fan, Z., Schatzberg, S. J., Styner, M. A., Flanigan, K. M., Xiao, X. & Hoffman, E. P., Feb 1 2012, In : Mammalian Genome. 23, 1-2, p. 85-108 24 p.

Research output: Contribution to journalArticle

Duchenne Muscular Dystrophy
Muscular Dystrophies
Therapeutic Uses
Canidae
Dystrophin
40 Citations

Enhancing muscle membrane repair by gene delivery of MG53 ameliorates muscular dystrophy and heart failure inδ-sarcoglycan-deficient hamsters

He, B., Tang, R. H., Weisleder, N., Xiao, B., Yuan, Z., Cai, C., Zhu, H., Lin, P., Qiao, C., Li, J., Mayer, C., Li, J., Ma, J. & Xiao, X., Jan 1 2012, In : Molecular Therapy. 20, 4, p. 727-735 9 p.

Research output: Contribution to journalArticle

Sarcoglycans
Muscular Dystrophies
Cricetinae
Heart Failure
Muscles
179 Citations

Phase 1 gene therapy for duchenne muscular dystrophy using a translational optimized AAV vector

Bowles, D. E., McPhee, S. W. J., Li, C., Gray, S. J., Samulski, J. J., Camp, A. S., Li, J., Wang, B., Monahan, P. E., Rabinowitz, J. E., Grieger, J. C., Govindasamy, L., Agbandje-Mckenna, M., Xiao, X. & Samulski, R. J., Jan 1 2012, In : Molecular Therapy. 20, 2, p. 443-455 13 p.

Research output: Contribution to journalArticle

Dependovirus
Duchenne Muscular Dystrophy
Capsid
Genetic Therapy
Arm
16 Citations

Single tyrosine mutation in AAV8 and AAV9 capsids is insufficient to enhance gene delivery to skeletal muscle and heart

Qiao, C., Yuan, Z., Li, J., Tang, R., Li, J. & Xiao, X., Feb 1 2012, In : Human gene therapy methods. 23, 1, p. 29-37 9 p.

Research output: Contribution to journalArticle

Capsid
Tyrosine
Skeletal Muscle
Mutation
Genes
2011
12 Citations

A versatile adeno-associated virus vector producer cell line method for scalable vector production of different serotypes

Yuan, Z., Qiao, C., Hu, P., Li, J. & Xiao, X., May 1 2011, In : Human Gene Therapy. 22, 5, p. 613-624 12 p.

Research output: Contribution to journalArticle

Dependovirus
Cell Line
Product Packaging
Transfection
Plasmids
118 Citations

Current status of pharmaceutical and genetic therapeutic approaches to treat DMD

Pichavant, C., Aartsma-Rus, A., Clemens, P. R., Davies, K. E., Dickson, G., Takeda, SI., Wilton, S. D., Wolff, J. A., Wooddell, C. I., Xiao, X. & Tremblay, J. P., Jan 1 2011, In : Molecular Therapy. 19, 5, p. 830-840 11 p.

Research output: Contribution to journalArticle

Dystrophin
Duchenne Muscular Dystrophy
Genetic Therapy
Pharmaceutical Preparations
Muscles
12 Citations

Delta-Sarcoglycan gene therapy halts progression of cardiac dysfunction, improves respiratory failure, and prolongs life in myopathic hamsters

Hoshijima, M., Hayashi, T., Jeon, Y. E., Fu, Z., Gu, Y., Dalton, N. D., Ellisman, M. H., Xiao, X., Powell, F. L. & Ross, J., Jan 1 2011, In : Circulation: Heart Failure. 4, 1, p. 89-97 9 p.

Research output: Contribution to journalArticle

Sarcoglycans
Cricetinae
Respiratory Insufficiency
Genetic Therapy
Myocardium
15 Citations

Directed evolution of adeno-associated virus (AAV) as vector for muscle gene therapy.

Yang, L., Li, J. & Xiao, X., Jul 12 2011, In : Methods in molecular biology (Clifton, N.J.). 709, p. 127-139 13 p.

Research output: Contribution to journalArticle

Dependovirus
Capsid
Genetic Therapy
Muscles
Genes
63 Citations

DOT1L regulates dystrophin expression and is critical for cardiac function

Nguyen, A. T., Xiao, B., Neppl, R. L., Kallin, E. M., Li, J., Chen, T., Wang, D. Z., Xiao, X. & Zhang, Y., Feb 1 2011, In : Genes and Development. 25, 3, p. 263-274 12 p.

Research output: Contribution to journalArticle

Dystrophin
Cardiac Myocytes
Dilated Cardiomyopathy
Methylation
Histones
69 Citations

Liver-specific microRNA-122 target sequences incorporated in AAV vectors efficiently inhibits transgene expression in the liver

Qiao, C., Yuan, Z., Li, J., He, B., Zheng, H., Mayer, C., Li, J. & Xiao, X., Apr 1 2011, In : Gene Therapy. 18, 4, p. 403-410 8 p.

Research output: Contribution to journalArticle

Dependovirus
MicroRNAs
Transgenes
Liver
Luciferases
42 Citations

One-year treatment of morpholino antisense oligomer improves skeletal and cardiac muscle functions in dystrophic mdx mice

Wu, B., Xiao, B., Cloer, C., Shaban, M., Sali, A., Lu, P., Li, J., Nagaraju, K., Xiao, X. & Lu, Q. L., Jan 1 2011, In : Molecular Therapy. 19, 3, p. 576-583 8 p.

Research output: Contribution to journalArticle

Inbred mdx Mouse
Morpholinos
Dystrophin
Myocardium
Skeletal Muscle
8 Citations

Phosphorylation of the anaphase-promoting complex/Cdc27 is involved in TGF-β signaling

Zhang, L., Fujita, T., Wu, G., Xiao, X. & Wan, Y., Mar 25 2011, In : Journal of Biological Chemistry. 286, 12, p. 10041-10050 10 p.

Research output: Contribution to journalArticle

Anaphase-Promoting Complex-Cyclosome
Phosphorylation
Transforming Growth Factor beta
Casein Kinase II
Chemical activation
8 Citations

Post-natal knockdown of fukutin-related protein expression in muscle by long-term RNA interference induces dystrophic pathology

Wang, C. H., Chan, Y. M., Tang, R. H., Xiao, B., Lu, P., Keramaris-Vrantsis, E., Zheng, H., Qiao, C., Jiang, J., Li, J., Ma, H. I., Lu, Q. & Xiao, X., Jan 1 2011, In : American Journal of Pathology. 178, 1, p. 261-272 12 p.

Research output: Contribution to journalArticle

Limb-Girdle Muscular Dystrophies
RNA Interference
Small Interfering RNA
Pathology
Muscles
36 Citations

Release of bioactive adeno-associated virus from fibrin scaffolds: Effects of fibrin glue concentrations

Lee, H. H., Haleem, A. M., Yao, V., Li, J., Xiao, X. & Chu, C. R., Aug 1 2011, In : Tissue Engineering - Part A. 17, 15-16, p. 1969-1978 10 p.

Research output: Contribution to journalArticle

Dependovirus
Fibrin Tissue Adhesive
Glues
Fibrin
Viruses
23 Citations

Single intra-articular injection of adeno-associated virus results in stable and controllable in vivo transgene expression in normal rat knees

Payne, K. A., Lee, H. H., Haleem, A. M., Martins, C., Yuan, Z., Qiao, C., Xiao, X. & Chu, C. R., Aug 1 2011, In : Osteoarthritis and Cartilage. 19, 8, p. 1058-1065 8 p.

Research output: Contribution to journalArticle

Intra-Articular Injections
Dependovirus
Transgenes
Viruses
Tetracycline
2010
47 Citations

Adeno-associated virus serotype 6 capsid tyrosine-to-phenylalanine mutations improve gene transfer to skeletal muscle

Qiao, C., Zhang, W., Yuan, Z., Shin, J. H., Li, J., Jayandharan, G. R., Zhong, L., Srivastava, A., Xiao, X. & Duan, D., Oct 1 2010, In : Human Gene Therapy. 21, 10, p. 1343-1348 6 p.

Research output: Contribution to journalArticle

Dependovirus
Capsid
Phenylalanine
Genetic Therapy
Tyrosine
17 Citations

Differential antitumor effect of interleukin-12 family cytokines on orthotopic hepatocellular carcinoma

Lo, C. H., Chang, C. M., Tang, S. W., Pan, W. Y., Fang, C. C., Chen, Y., Wu, P. Y., Chen, K. Y., Ma, H. I., Xiao, X. & Tao, M. H., May 1 2010, In : Journal of Gene Medicine. 12, 5, p. 423-434 12 p.

Research output: Contribution to journalArticle

Interleukin-12
Dependovirus
Hepatocellular Carcinoma
Interleukin-27
Interleukin-23
288 Citations

Dystrophin immunity in Duchenne's muscular dystrophy

Mendell, J. R., Campbell, K., Rodino-Klapac, L., Sahenk, Z., Shilling, C., Lewis, S., Bowles, D., Gray, S., Li, C., Galloway, G., Malik, V., Coley, B., Clark, K. R., Li, J., Xiao, X., Samulski, J., McPhee, S. W., Samulski, R. J. & Walker, C. M., Oct 7 2010, In : New England Journal of Medicine. 363, 15, p. 1429-1437 9 p.

Research output: Contribution to journalArticle

Dystrophin
Duchenne Muscular Dystrophy
Immunity
T-Lymphocytes
Transgenes
29 Citations

Efficient retrograde transport of adeno-associated virus type 8 to spinal cord and dorsal root ganglion after vector delivery in muscle

Zheng, H., Qiao, C., Wang, C. H., Li, J., Li, J., Yuan, Z., Zhang, C. & Xiao, X., Jan 1 2010, In : Human Gene Therapy. 21, 1, p. 87-97 11 p.

Research output: Contribution to journalArticle

Dependovirus
Spinal Nerve Roots
Spinal Ganglia
Spinal Cord
Muscles
24 Citations

Expression of dog microdystrophin in mouse and dog muscles by gene therapy

Pichavant, C., Chapdelaine, P., Cerri, D. G., Dominique, J. C., Quenneville, S. P., Skuk, D., Kornegay, J. N., Bizario, J. C., Xiao, X. & Tremblay, J. P., May 1 2010, In : Molecular Therapy. 18, 5, p. 1002-1009 8 p.

Research output: Contribution to journalArticle

Genetic Therapy
Duchenne Muscular Dystrophy
Dogs
Muscles
Dystrophin
21 Citations

Improvement of the mdx mouse dystrophic phenotype by systemic in utero AAV8 delivery of a minidystrophin gene

Koppanati, B. M., Li, J., Reay, D. P., Wang, B., Daood, M., Zheng, H., Xiao, X., Watchko, J. F. & Clemens, P. R., Nov 1 2010, In : Gene Therapy. 17, 11, p. 1355-1362 8 p.

Research output: Contribution to journalArticle

Inbred mdx Mouse
Dystrophin
Duchenne Muscular Dystrophy
Skeletal Muscle
Phenotype