• 2178 Citations
  • 22 h-Index
19982019
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  • 6 Similar Profiles
Dependovirus Medicine & Life Sciences
Genetic Therapy Medicine & Life Sciences
Genes Medicine & Life Sciences
Giant Axonal Neuropathy Medicine & Life Sciences
Central Nervous System Medicine & Life Sciences
Globoid Cell Leukodystrophy Medicine & Life Sciences
Transgenes Medicine & Life Sciences
Motor Neurons Medicine & Life Sciences

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Projects 2008 2019

Giant Axonal Neuropathy
Intermediate Filaments
Genetic Therapy
Motor Neurons
Sensory Receptor Cells
Genetic Therapy
Central Nervous System
Genes
Cerebrospinal Fluid
Giant Axonal Neuropathy

INCL Gene Therapy Project Support

Gray, S. J.

Taylors Tale

5/1/153/3/17

Project: Research project

Giant Axonal Neuropathy
Genetic Therapy
Genetic Databases
Intermediate Filaments
Polyneuropathies

Research Output 1998 2018

  • 2178 Citations
  • 22 h-Index
  • 43 Article
  • 10 Review article
  • 4 Comment/debate
1 Citations

Development of Intrathecal AAV9 Gene Therapy for Giant Axonal Neuropathy

Bailey, R. M., Armao, D., Nagabhushan Kalburgi, S. & Gray, S. J. Jun 15 2018 In : Molecular Therapy - Methods and Clinical Development. 9, p. 160-171 12 p.

Research output: Contribution to journalArticle

Giant Axonal Neuropathy
Genetic Therapy
Intermediate Filaments
Clinical Trials, Phase I
Viral Genes

Long-Term Improvement of Neurological Signs and Metabolic Dysfunction in a Mouse Model of Krabbe's Disease after Global Gene Therapy

Marshall, M. S., Issa, Y., Jakubauskas, B., Stoskute, M., Elackattu, V., Marshall, J. N., Bogue, W., Nguyen, D., Hauck, Z., Rue, E., Karumuthil-Melethil, S., Zaric, V., Bosland, M., van Breemen, R. B., Givogri, M. I., Gray, S. J., Crocker, S. J. & Bongarzone, E. R. Mar 7 2018 In : Molecular Therapy. 26, 3, p. 874-889 16 p.

Research output: Contribution to journalArticle

Psychosine
Galactosylceramidase
Globoid Cell Leukodystrophy
Oligodendroglia
Microglia

Recent progress and considerations for AAV gene therapies targeting the central nervous system

Lykken, E. A., Shyng, C., Edwards, R. J., Rozenberg, A. & Gray, S. J. May 18 2018 In : Journal of Neurodevelopmental Disorders. 10, 1, 16

Research output: Contribution to journalReview article

Dependovirus
Gene Targeting
Genetic Therapy
Central Nervous System
Therapeutics
8 Citations

Development of a Novel AAV Gene Therapy Cassette with Improved Safety Features and Efficacy in a Mouse Model of Rett Syndrome

Gadalla, K. K. E., Vudhironarit, T., Hector, R. D., Sinnett, S., Bahey, N. G., Bailey, M. E. S., Gray, S. J. & Cobb, S. R. Jun 16 2017 In : Molecular Therapy - Methods and Clinical Development. 5, p. 180-190 11 p.

Research output: Contribution to journalArticle